Fetal therapy for congenital hydrocephalus—where we came from and where we are going
Sign Up to like & getrecommendations! Published in 2020 at "Child's Nervous System"
DOI: 10.1007/s00381-020-04738-9
Abstract: Despite unfavorable outcomes during the early experience with in utero intervention for congenital hydrocephalus, improvements in prenatal diagnosis, patient selection, and fetal surgery techniques have led to a renewed interest in fetal intervention for congenital… read more here.
Keywords: congenital hydrocephalus; therapy congenital; fetal therapy; hydrocephalus came ... See more keywords
The evolving landscape of gene therapy for congenital haemophilia: An unprecedented, problematic but promising opportunity for worldwide clinical studies.
Sign Up to like & getrecommendations! Published in 2020 at "Blood reviews"
DOI: 10.1016/j.blre.2020.100737
Abstract: With liver-directed gene therapy, congenital haemophilia has the potential to progress from an incurable to a phenotypically curable condition. However, the proportion of haemophilia population likely to benefit from gene therapy remains to be established.… read more here.
Keywords: gene; gene therapy; congenital haemophilia; therapy congenital ... See more keywords