Gene therapy decreases seizures in a model of Incontinentia pigmenti
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DOI: 10.1002/ana.24981
Abstract: Incontinentia pigmenti (IP) is a genetic disease leading to severe neurological symptoms, such as epileptic seizures, but no specific treatment is available. IP is caused by pathogenic variants that inactivate the Nemo gene. Replacing Nemo… read more here.
Keywords: therapy decreases; gene therapy; incontinentia pigmenti; gene ... See more keywords