Developments in FGFR and IDH inhibitors for cholangiocarcinoma therapy
Sign Up to like & getrecommendations! Published in 2023 at "Expert Review of Anticancer Therapy"
DOI: 10.1080/14737140.2023.2176846
Abstract: ABSTRACT Introduction Cholangiocarcinoma (CCA) is an uncommon malignancy originating from epithelial cells of the biliary tract. Regardless of the site of origin within the biliary tree, CCAs are generally aggressive with a poor survival. Surgical… read more here.
Keywords: inhibitors cholangiocarcinoma; therapy; idh inhibitors; therapy developments ... See more keywords
Gene Therapy Developments for Pompe Disease
Sign Up to like & getrecommendations! Published in 2022 at "Biomedicines"
DOI: 10.3390/biomedicines10020302
Abstract: Pompe disease is an inherited neuromuscular disorder caused by deficiency of the lysosomal enzyme acid alpha-glucosidase (GAA). The most severe form is infantile-onset Pompe disease, presenting shortly after birth with symptoms of cardiomyopathy, respiratory failure… read more here.
Keywords: pompe disease; therapy developments; therapy; gene therapy ... See more keywords