Lentiviral Gene Therapy for X-Linked Chronic Granulomatous Disease
Sign Up to like & getrecommendations! Published in 2020 at "Pediatrics"
DOI: 10.1542/peds.2020-023861rrrr
Abstract: DB Kohn, C Booth, EM Kang. Nature Med. 2020;26(2):200–206 To assess the safety and evaluate the efficacy and stability of ex vivo autologous CD34+ hematopoietic stem and progenitor cell based lentiviral gene therapy for X-linked… read more here.
Keywords: linked chronic; lentiviral gene; gene therapy; therapy linked ... See more keywords
Advances in Gene Therapy for X-Linked Myotubular Myopathy: Current Progress and Future Challenges.
Sign Up to like & getrecommendations! Published in 2025 at "Current gene therapy"
DOI: 10.2174/0115665232388661250430062849
Abstract: read more here.
Keywords: linked myotubular; therapy linked; gene therapy; gene ... See more keywords