Gene therapy for neurotransmitter‐related disorders
Sign Up to like & getrecommendations! Published in 2024 at "Journal of Inherited Metabolic Disease"
DOI: 10.1002/jimd.12697
Abstract: Inborn errors of neurotransmitter (NT) metabolism are a group of rare, heterogenous diseases with predominant neurological features, such as movement disorders, autonomic dysfunction, and developmental delay. Clinical overlap with other disorders has led to delayed… read more here.
Keywords: therapy neurotransmitter; gene therapy; related disorders; neurotransmitter related ... See more keywords