Metachromatic leukodystrophy and transplantation: remyelination, no crossâcorrection
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DOI: 10.1002/acn3.50975
Abstract: In metachromatic leukodystrophy, a lysosomal storage disorder due to decreased arylsulfatase A activity, hematopoietic stem cell transplantation may stop brain demyelination and allow remyelination, thereby halting white matter degeneration. This is the first study to… read more here.
Keywords: metachromatic leukodystrophy; transplantation remyelination; leukodystrophy transplantation; leukodystrophy ... See more keywords