Diagnosis and New Treatment Avenues in Spinal Muscular Atrophy
Sign Up to like & getrecommendations! Published in 2017 at "Neuropediatrics"
DOI: 10.1055/s-0037-1603517
Abstract: Abstract Spinal muscular atrophy (SMA) is an autosomal‐recessive, neuromuscular disorder that is characterized by degeneration of the anterior horn cells of the spinal cord, resulting in muscle atrophy and proximal muscle weakness. SMA is caused… read more here.
Keywords: treatment avenues; muscle; spinal muscular; treatment ... See more keywords
Gangliosides: Treatment Avenues in Neurodegenerative Disease
Sign Up to like & getrecommendations! Published in 2019 at "Frontiers in Neurology"
DOI: 10.3389/fneur.2019.00859
Abstract: Gangliosides are cell membrane components, most abundantly in the central nervous system (CNS) where they exert among others neuro-protective and -restorative functions. Clinical development of ganglioside replacement therapy for several neurodegenerative diseases was impeded by… read more here.
Keywords: treatment avenues; avenues neurodegenerative; gangliosides treatment; disease ... See more keywords